Abstracts will be published in BMJ Paediatrics Open

CONGRESS COURSES


COURSE 1 - CASE BASED NEONATAL MECHANICAL VENTILATION COURSE
Date : 17 April 2024
Time : 14:00 – 18:40
Meeting Room : Course Meeting Room
Seats Available : 50
Course Registration Fee: EURO 20 included vat. (Congress Registration is Mandatory to Participate in the Courses)

14:00 - 14:40 Physiology of Newborn Respiration
İlke Mungan Akın
14:40 - 15:00 Break
15:00 - 15:40 Non-Invasive Ventilation
Evrim Kıray Baş
15:40 - 16:00 Break
16:00 - 16:40 Conventional Mechanical Ventilation
Tuğba Erener Ercan
16:40 - 17:00 Break
17:00 - 17:40 New Modes of Mechanical Ventilation
Zeynep Alp Ünkar
17:40 - 18:00 Break
18:00 - 18:40 Follow Up of Newborn Receiving Mechanical Ventilation
Ersin Ulu


COURSE 2 - NEW AND UPCOMING TREATMENTS FOR RARE DISEASES COURSE
Date : 17 April 2024
Time : 14:00 – 20:15
Meeting Room : Course Meeting Room
Seats Available : 50
Course Registration Fee: Included in congress registration fee. (Congress Registration is Mandatory to Participate in the Courses)

Course Coordinator: Fatih Ezgü
14.00 - 14:15 Welcome and Introduction
Mehmet Vural
Point to be Covered
• Introduction of the Agenda
14:15 - 14:30 General Overview of Rare Diseases and Their Treatments in the “0mics” Era
Yasemin Alanay
Point to be Covered
• Definition of Rare Disease
• Emerging Needs for Treatment
• Current Status of Research and Approved Treatments
14:30 - 14:45 Advancements in Pre-clinical Drug Development for Rare Diseases
Fatih Ezgü
Point to be Covered
• Wet-lab Techniques for Drug Development
• Virtual Techniques for Drug Development
14:45 - 15:00 Clinical Trials for Rare Diseases
Fatih Ezgü
Point to be Covered
• End-points for Clinical Trials
• Types of Clinical Trials
15:00 - 15:15 Enzyme Replacement Therapy and Sphingomyelinase Deficiency as an Example
Sema Kalkan Uçar
Point to be Covered
• General Overview of ERTs
• General Introduction of NPD
• Efficacy and Safety of Olipudase Alfa
15:15 - 15:30 Q&A
15:30 - 16:15 LUNCH
16:15 - 16:30 General Introduction to AAV Based Gene Therapy and AADC Deficiency as an Example of Targeted Application
Fatih Ezgü
Point to be Covered
• Introduction to AAV based gene therapy
• İmmune reactions
• AADC deficiency as an targeted application
16:30 - 16:45 Gene Therapy for Haemophilia: An example of Systemic Application
Kaan Kavaklı
Point to be Covered
• Efficacy and Safety of Gene Therapy for Haemophilia
16:45 - 17:00 Approved and Upcoming Treatments for Skeletal Dysplasias
Yasemin Alanay
Point to be Covered
• Efficacy and Safety of Voxzogo for Achondroplasia
• Research for New Treatment Options
17:00 - 17:15 New Treatments for SMA
Uluç Yiş
Point to be Covered
• Efficacy and Safety of Gene and Other Therapies for SMA
17:15 - 17:30 Q&A
17:30 - 18:00 Break
18:00 - 18:15 Upcoming Treatments for Rare Diseases
Fatma Derya Bulut
Point to be Covered
• Discuss About Recent Search for the Treatment of Rare Diseases
18:15 - 18:30 Idebenone Treatment for Leber’s Hereditary Optic Neuropathy
Melike Ersoy
18:30 - 18:45 Safety and Efficacy of Velmanase Alfa for the Treatment of Mannosidosis
Fatih Ezgü
18:45 - 19:00 Q&A
19:00 - 19:30 Break
19:30 - 19:45 Enzyme Replacement Therapy for ADA-SCID. What Do We Know Up to Now?
Deniz Çağdaş Ayvaz
19:45 - 20:00 Q&A
20:00 - 20:15 Wrap Up
Mehmet Vural


COURSE 3 - PEDIATRIC EMERGENCY & CRITICAL CARE COURSE (PEDECC) BY EPA – UNEPSA PRACTICAL SESSIONS
Date : 17 April 2024
Time : 14:00 – 19:15
Meeting Room : Course Meeting Room
Seats Available : 50
Course Registration Fee: EURO 20 included vat. (Congress Registration is Mandatory to Participate in the Courses)

Course Coordinators: Ebru Atike Ongun, Alper Köker, Esra Şevketoğlu
14:00 - 14:15 INTRODUCTION & OPENING
Massimo Pettoello Mantovani, Mehmet Vural, Esra Şevketoğlu
14:15 - 15:15 PRACTICAL SESSIONS

* BASIC LIFE SUPPORT
Emel Ulusoy, Ebru Atike Ongun, Alper Köker, Emin Menentoğlu

* AIRWAY MANAGEMENT
İrem Sofuoğlu, Hakan Tekgüç, Merve Havan, Erdem Çebişli
15:15 - 15:30 Break
15:30 - 16:30 PRACTICAL SESSIONS

* PEDIATRIC SHOCK MANAGEMENT
Mustafa Çolak, Nagehan Aslan, Ayla Akça Çağlar, Tolga Besci

* RHYTHM DISTURBANCES IN CHILDREN
Emel Ulusoy, Tolga Besci, İrem Sofuoğlu, Hakan Tekgüç
16:30 - 17:30 PRACTICAL SESSIONS

* ESSENTIALS OF PEDIATRIC DIAGNOSTIC IMAGING
Ayla Akca Çağlar, Nagehan Aslan, Merve Havan

* APPROACH TO TRAUMA
Ebru Atike Ongun, Alper Köker, Mustafa Çolak, Emin Menentoğlu, Erdem Çebişli
17:30 - 17:45 Break
17:45 - 18:45 COURSE EXAM
18:45 - 19:15 CERTIFICATION & CLOSING CEREMONY